Presenting Author: Giorgia Zanetti – Columbia University
###Speaker: Pere Santamaria, MD, PhD (he/him/his) – University of Calgary
### he/him/hisSpeaker: Luigi Naldini, MD, PhD (he/him/his) – San Raffaele Telethon Institute for Gene Therapy (SR-Tiget)
### he/him/hisPresenting Author: Daniela Fernandez-Salinas, BSc (she/her/hers) – Boston Children's Hospital
### she/her/hersPresenting Author: Betul Melike Ogan, MSc (she/her/hers) – Institute of Molecular Genetics of the Czech Academy of Sciences
### she/her/hersSpeaker: Antoine Roquilly, MD,PhD (he/him/his) – Nantes University
### he/him/his